Molecular Genetics and Metabolism

Impact of elosulfase alfa in patients with Morquio syndrome type A who have limited ambulation: An open-label, phase 2 study.

Molecular Genetics and Metabolism

Paul R. Harmatz, Andrea Jester, Eugen Mengel, Marsha Treadwell, Barbara K. Burton, Kenneth I. Berger, Christian J. Hendriksz, Tarekegn Geberhiwot, Zlatko Sisic, Celeste Decker

Impact of elosulfase alfa on pain in patients with Morquio syndrome type A.

Molecular Genetics and Metabolism

Paul Harmatz, M. Treadwell, Barbara K. Burton, John Mitchell, N. Muschol, Simon Jones, Gregory Pastores, Heather Lau, R. Sparkes, V.R. Sutton, F. Genter, C. Haller, A. Shaywitz