Clinical TrialsNeha Bhasin, MD Ellen Fung, PhD Robert Hagar, MD Shannon Kelly, MD Ashutosh Lal, MD Elliott Vichinsky, MDMadhav Vissa, MDGene TherapyMark Walters, MDImplementation Marsha Treadwell, PhDInternational Shannon Kelly, MDAshutosh Lal, MDMarsha Treadwell, PhDIn the Lab Frans Kuypers, PhDAngela Rivers, MD